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Cure Sanfilippo Foundation is a Not-for-Profit organization. All net funding goes to the urgent mission to advance treatment options to treat children with Sanfilippo. This is led by proactive families of children with Sanfilippo Syndrome, and their supporters, who work tirelessly to change the fate and future for these children.
Our Mission Is Simple:
To advocate for and fund research directed towards a cure and treatment options for patients with Sanfilippo Syndrome.
Cure Sanfilippo conducts and funds promising research, projects, and clinical trials. Learn more about our research efforts.
Together, a cure comes sooner. We collaborate with families, researchers, academic institutions, regulators, and bio-technology companies.
Cure Sanfilippo connects families globally with the latest information on current research, as well as provides support for fundraising and caring for their children.
We set ambitious annual fundraising goals in order to fund research for every kind of Sanfilippo and to dictate and accelerate the pace of research.
The more people who know about Sanfilippo, the more progress that happens to find a cure. So we help elevate awareness of Sanfilippo.
H4B Boston’s Living Rooms of RareIn celebration of Rare Disease Day, H4B ...
Raising an Adult Child With Sanfilippo Syndrome Is TiringI am tired. Caring for my 25-year-old da...
An Observational, Prospective, Multicenter, Natural History Study of Patients With Mucopolysaccharidosis Type IIIAMucopolysaccharidosis type IIIA (MPS III...
A Guide to Understanding MPS III (Sanfilippo Syndrome)MPS III belongs to a group of inherited ...
Differences in Gene Expression Patterns, Revealed by RNA-Seq Analysis, Between Various Sanfilippo and Morquio Diseas...Mucopolysaccharidoses (MPS) are genetic ...
I Want to Live in the Moment While There’s Still TimeMy daughter Abby has Sanfilippo syndrome...
Terri L. Klein Received the WORLDSymposium 2021 Patient Advocate Leader (PAL) AwardTerri is a founding member of the Mucoli...