Trusted Resources: People & Places
Online groups, photo galleries and blogs
Cure Sanfilippo Foundation is a Not-for-Profit organization. All net funding goes to the urgent mission to advance treatment options to treat children with Sanfilippo. This is led by proactive families of children with Sanfilippo Syndrome, and their supporters, who work tirelessly to change the fate and future for these children.
Our Mission Is Simple:
To advocate for and fund research directed towards a cure and treatment options for patients with Sanfilippo Syndrome.
Accelerate Research:
Cure Sanfilippo conducts and funds promising research, projects, and clinical trials. Learn more about our research efforts.
Drive Collaboration:
Together, a cure comes sooner. We collaborate with families, researchers, academic institutions, regulators, and bio-technology companies.
Support/Unite Families:
Cure Sanfilippo connects families globally with the latest information on current research, as well as provides support for fundraising and caring for their children.
Raise Funds:
We set ambitious annual fundraising goals in order to fund research for every kind of Sanfilippo and to dictate and accelerate the pace of research.
Increase Awareness:
The more people who know about Sanfilippo, the more progress that happens to find a cure. So we help elevate awareness of Sanfilippo.
Related Content
-
Losing Stanley – My Little Boy Doesn’t Recognise Me AnymoreLittle Stanley Barnes was diagnosed with...
-
Long-Term Safety and Clinical Outcomes of Intrathecal Heparan-N-Sulfatase in Patients With Sanfilippo Syndrome Type ...Currently, there is no effective therapy...
-
MPS IIIA (Sanfilippo Syndrome, Type A) in a 7-Year-Old Girlhttps://slideplayer.com/slide/13595382/...
-
Stuart SiedmanStuart is the Global Head of Patient Adv...
-
Electroclinical Features of Epilepsy in Mucopolysaccharidosis III: Outcome Description in a Cohort of 15 Italian Pat...Mucopolysaccharidosis III (Sanfilippo sy...
-
H4B Boston’s Living Rooms of RareIn celebration of Rare Disease Day, H4B ...
-
A Guide to Understanding MPS III (Sanfilippo Syndrome)MPS III belongs to a group of inherited ...