Mucopolysaccharidosis VII Disease Monitoring Program
study id #: NCT03604835
condition: Mucopolysaccharidosis VII, MPS VII, MPS 7, Sly Syndrome
status: Recruiting
purpose:The objectives of this study are to characterize MPS VII disease presentation and progression and assess long-term effectiveness and safety, including hypersensitivity reactions and immunogenicity of vestronidase alfa.
intervention: No Intervention
results: https://clinicaltrials.gov/ct2/show/results/NCT03604835
last updated: February 26, 2022
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