A Long-Term Follow-Up Study of Patients With MPS IIIB Treated With ABO-101

key information

study id #: NCT04655911

condition: Mucopolysaccharidosis III-B

status: Recruiting


This is a multicenter, non-interventional, long-term follow-up (LTFU) study in participants who have been treated with ABO-101 in a prior trial. Eligible participants will undergo clinical evaluations at prespecified intervals for 3 years from the last visit in the prior clinical trial (up to 5 years post-treatment).

intervention: ABO-101


last updated: February 26, 2022