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Disease Burden, Management Patterns and Multidisciplinary Clinical Approaches for Patients With MPS IVA and VI in Selected Latin American Countries
source: Molecular genetics and metabolism reports
year: 2021
authors: Solano VM,Mandujano CYC,Avila-Rejon CA,Espin VH,Montaño HPQ
summary/abstract:There is a paucity of real-world epidemiological data on patients with mucopolysaccharidoses (MPS) in Latin America. This real-world study assessed the disease burden, management patterns and multidisciplinary clinical approaches for MPS-IVA and MPS-VI patients in Latin America (Colombia, Ecuador, Mexico, Peru).
organization: Fundación Cardioinfantil, Bogota, Colombia.DOI: 10.1016/j.ymgmr.2021.100769
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