An Extension Study of JR-171-101 Study in Patients With MPS I
study id #: NCT04453085
condition: Mucopolysaccharidosis I
status: Recruiting
purpose:Phase I/II, open label, multicenter, multinational (Japan, Brazil and the US) extension study of JR-171-101 for the treatment of MPS I
intervention: JR-171
results: https://clinicaltrials.gov/ct2/show/results/NCT04453085
last updated: February 26, 2022
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