Trusted Resources: People & Places
Online groups, photo galleries and blogs
Jackie James
President Cure Mucolipidosis
402 Park Avenue
Belleville, Illinois, United States
Jackie is the mother of Anna who has Mucolipidosis III alpha/beta. Jackie began her journey into advocating for rare disease in 2012 when she joined the board of ISMRD. In 2015, Jackie stepped up as the board President of ISMRD and spent several years working with the board advocating for Mucolipidosis and several other rare diseases.
Jackie has spent the last 14 years managing her family business and brings her business skills to the table to work with the board and accomplish the mission and vision that defines Cure Mucolipidosis. She is very much looking forward to seeing the science and research develop and ultimately see a cure/treatment for Mucolipidosis.
BookmarkRelated Content
-
Clinical and Event-Based Outcomes of Patients With Mucopolysaccharidosis VI Receiving Enzyme Replacement Therapy in ...The objective of this study was to descr...
-
Europe Grants Orphan Drug Status to JR-441, ERT for Sanfilippo AThe European Commission has granted an o...
-
Patricia Dickson, MDDr. Dickson is Division Chief of Genetic...
-
Treatment of Skeletal and Non-Skeletal Alterations of Mucopolysaccharidosis Type IVA by AAV-Mediated Gene TherapyMucopolysaccharidosis type IVA (MPSIVA) ...
-
Gene Therapy for Neuronopathic Mucopolysaccharidoses: State of the ArtThe need for long-lasting and transforma...
-
A Guide to Understanding MPS III (Sanfilippo Syndrome)MPS III belongs to a group of inherited ...
-
Are You Considering Stem Cell Transplantation? Questions to Ask Your ProviderStem cell transplantation can be an over...
